Every time a shuttle docks with the International Space Station (ISS), a delicate dance unfolds between the shuttle's docking ...

These unique, branched molecules help LNPs break through the endosomal membrane, making them more effective at delivering mRNA and gene-editing tools. In a recent study in Nature Communications ...

This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...

Genetic medicines could treat certain diseases, however, the current delivery systems available—viral vectors and lipid nanoparticles (LNPs)—pose unique challenges for gene therapy applications. For ...

RFK Jr.'s comments about the gene-editing technology raise a question about how he would regulate it as head of HHS.

Akribion Therapeutics emerges from stealth with €8 million in seed funding to develop a novel cancer RNA-guided approach ...

In trials at University College London Hospitals (UCLH), an ASO is being used to target the mutated gene that results in the ...

Pluristyx, a leading provider of innovative, unmodified, and gene-edited induced pluripotent stem cell (iPSC) lines, submitted a Type II Drug Master File (DMF) to the U.S. Food and Drug Administration ...

Could viral infections play a role in Huntington's disease? Research suggests Apolipoprotein B mRNA editing catalytic ...

People genetically susceptible to Huntington's disease often see their movement, mood, and cognition decline slowly over time.

These unique, branched molecules help LNPs break through the endosomal membrane, making them more effective at delivering mRNA and gene-editing tools. In a recent study in Nature Communications ...