In surveys, parents of children with SMA and healthcare professionals in Sweden note the many ways the pandemic affected ...

Scholar Rock is asking the U.S. Food and Drug Administration to approve apitegromab for people with spinal muscular atrophy.

Problems with chemical messengers like dopamine were tied to posture issues in SMA in a mouse study, but levodopa therapy may ...

Inclement weather can pose a threat to people like columnist Ari Anderson, who depend on in-home care. Such are the storms of ...

Columnist Helen Baldwin gains a different perspective following a crushing diagnosis, but glasses weren't what helped her to see clearly.