Over the last few months, our Living with LHON features have looked at the individual stories of the inspirational people who have refused to let sight loss mean the end of their dreams.

In the case of a rare disease like Leber’s Hereditary Optic Neuropathy (LHON), those tools can be few and far between, making it even harder for patients to plot the best course for them.

LHON is a relatively rare genetic disorder of ... The trial was carried out at sites across the UK, Europe, the US and Taiwan, seeing up to 98 subjects between 2018 and 2019.

GenSight Biologics’ lead product candidate, GS010, is in Phase III trials in Leber Hereditary Optic Neuropathy (LHON), a rare mitochondrial disease that leads to irreversible blindness in teens ...